|
Gene Therapy
Citations 271-280 of 434 total displayed.
|
Past content
(since Aug 1998):
|
In utero gene transfer of human factor IX to fetal mice can induce postnatal tolerance of the exogenous clotting factor
- Simon N. Waddington, Suzanne M. K. Buckley, Megha Nivsarkar, Sarah Jezzard, Holm Schneider, Thomas Dahse, Geoff Kemball-Cook, Maznu Miah, Nick Tucker, Margaret J. Dallman, Mike Themis, and Charles Coutelle
Blood 2003; 101: 1359-1366.
[Abstract]
[Full text]
[PDF]
LCR-regulated transgene expression levels depend on the Oct-1 site in the AT-rich region of  -globin intron-2
- Rikki R. Bharadwaj, Cecelia D. Trainor, Peter Pasceri, and James Ellis
Blood 2003; 101: 1603-1610.
[Abstract]
[Full text]
[PDF]
A CD45 minigene restores regulated isoform expression and immune function in CD45-deficient mice: therapeutic implications for human CD45-null severe combined immunodeficiency
- Elizabeth L. Virts, Oscar Diago, and William C. Raschke
Blood 2003; 101: 849-855.
[Abstract]
[Full text]
[PDF]
CD28 costimulation and immunoaffinity-based selection efficiently generate primary gene-modified T cells for adoptive immunotherapy
- Carolina Berger, C. Anthony Blau, Tim Clackson, Stanley R. Riddell, and Shelly Heimfeld
Blood 2003; 101: 476-484.
[Abstract]
[Full text]
[PDF]
Gene therapy of apolipoprotein E-deficient mice using a novel macrophage-specific retroviral vector
- Peter J. Gough and Elaine W. Raines
Blood 2003; 101: 485-491.
[Abstract]
[Full text]
[PDF]
High-level expression of hemoglobin A in human thalassemic erythroid progenitor cells following lentiviral vector delivery of an antisense snRNA
- Marla M. Vacek, Hong Ma, Federica Gemignani, Giuseppina Lacerra, Tal Kafri, and Ryszard Kole
Blood 2003; 101: 104-111.
[Abstract]
[Full text]
[PDF]
Third-generation, self-inactivating gp91phox lentivector corrects the oxidase defect in NOD/SCID mouse-repopulating peripheral blood-mobilized CD34+ cells from patients with X-linked chronic granulomatous disease
- Joachim Roesler, Sebastian Brenner, Anatoly A. Bukovsky, Narda Whiting-Theobald, Thomas Dull, Michael Kelly, Curt I. Civin, and Harry L. Malech
Blood 2002; 100: 4381-4390.
[Abstract]
[Full text]
[PDF]
Lentiviral gene transfer and ex vivo expansion of human primitive stem cells capable of primary, secondary, and tertiary multilineage repopulation in NOD/SCID mice
- Wanda Piacibello, Stefania Bruno, Fiorella Sanavio, Sara Droetto, Monica Gunetti, Laurie Ailles, Francesca Santoni de Sio, Andrea Viale, Loretta Gammaitoni, Angelo Lombardo, Luigi Naldini, and Massimo Aglietta
Blood 2002; 100: 4391-4400.
[Abstract]
[Full text]
[PDF]
Transgenic targeting with regulatory elements of the human CD34 gene
- Hanna S. Radomska, David A. Gonzalez, Yutaka Okuno, Hiromi Iwasaki, Andras Nagy, Koichi Akashi, Daniel G. Tenen, and Claudia S. Huettner
Blood 2002; 100: 4410-4419.
[Abstract]
[Full text]
[PDF]
Distal elements are critical for human CD34 expression in vivo
- Yutaka Okuno, Claudia S. Huettner, Hanna S. Radomska, Victoria Petkova, Hiromi Iwasaki, Koichi Akashi, and Daniel G. Tenen
Blood 2002; 100: 4420-4426.
[Abstract]
[Full text]
[PDF]
|
|
